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Bya deficiency (1) |
Efficacy (1) |
Elosulfase alfa treatment (1) |
Enzyme replacement therapy (1) |
GALNS (1) |
Lysosomal storage disorder (1) |
Morquio A syndrome (1) |
MPS IVA (1) |
Mucopolysaccharidosis (1) |
Pharmacodynamics (1) |
Pharmacokinetics (1) |
Safety and tolerability (1) |
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