Guest, Julian F.; Ingram, Andy; Ayoub, Nadia; Hendriksz, Christian J.; Murphy, Elaine; Rahman, Yusof; McKiernan, Patrick; Mundy, Helen; Deegan, Patrick
(Public Library of Science, 2018-02-02)
OBJECTIVE : To estimate clinical progression and resource utilisation together with the associated costs
of managing children and adults with LAL Deficiency, at a tertiary referral centre in the UK. METHODS : A retrospective ...