Stefanutti, Claudia; Blom, Dirk J.; Averna, Maurizio R.; Meagher, Emma A.; Theron, Hendrik Du Toit; Marais, A. David; Hegele, Robert A.; Sirtori, Cesare R.; Shah, Prediman K.; Gaudet, Daniel; Vigna, Giovanni B.; Sachais, B.S.; Di Giacomo, S.; Du Plessis, Anna M.E.; Bloeden, LeAnne T.; Balser, J.; Rader, Daniel J.; Cuchel, Marina
(Elsevier, 2015-06)
OBJECTIVE : Lomitapide (a microsomal triglyceride transfer protein inhibitor) is an adjunctive treatment
for homozygous familial hypercholesterolaemia (HoFH), a rare genetic condition characterised by
elevated low-density ...